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Mucopolysaccharidosis III - 25 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: Biomarker for Sanfilippo Disease Condición:
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Enrolling by invitation |
Nombre del estudio: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. Condición:
Fecha: 2015-01-21 Intervenciones: Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |
Recruiting |
Nombre del estudio: A Treatment Study of Mucopolysaccharidosis Type IIIB Condición:
Fecha: 2016-02-27 Intervenciones: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
Nombre del estudio: Neurobehavioral Phenotypes in MPS III Condición:
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Completed |
Nombre del estudio: Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using Multimodal Magnetic Resonance Imaging Condición: MPS IIIB (Sanfilippo B Syndrome) Fecha: 2014-03-12 |
Recruiting |
Nombre del estudio: A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB) Condición:
Intervenciones: Other: This is an observational study This is an observational study |